Treatment Options for Niemann-Pick Type C

Elizabeth Berry-Kravis, MD, PhD, co-director of the Molecular Diagnostics Section of the Genetic Laboratory at Rush Medical College in Chicago, describes dif

NPC PFDD - Overview of Niemann-Pick Type C Disease and Current Treatments

Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a Neuronal-Like Cell Model of Niemann–Pick Type C Using Quantitative Proteomics

Advancing diagnosis and treatment of Niemann-Pick C disease through biomarker discovery

Niemann-Pick disease type C as a neurovisceral disease. Schematic

Protocol for initiation of miglustat treatment in NP-C. Reproduced with

Niemann-Pick disease type C

Niemann-Pick Disease Type C

Niemann-Pick disease type C: Video & Anatomy

FDA says Hold Off on Zavesca (Miglustat) approval. « Niemann-Pick Children's Fund, Inc

Summer 2022 Newsletter – NNPDF

Niemann–Pick disease type C Therapeutics Market - NPC Therapeutics Market